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2 résultats trouvés

Dynamic palmitoylation regulates TDP-43 nucleocytoplasmic transport in ALS

Common features in amyotrophic lateral sclerosis (ALS) include misdirected proteins that build up over time and lead to large protein clumps that are toxic to the cell and lead to cell death.


TYPE DE SUBVENTION
Subventions d'équipe
Domaine de recherche
Neurodégénérescence
Province
Québec
DATE DE DÉBUT
2024

A unifying approach to treat multisystem proteinopathy and ALS using noninvasive novel ASO delivery

Multisystem proteinopathy (MSP) is a devastating rare disease described by a cluster of diseases that affect the brain, bone, and muscle.


TYPE DE SUBVENTION
Subventions pour le renforcement des capacités
Domaine de recherche
Neurodégénérescence
Concours
Les futurs leaders de la recherche sur le cerveau au Canada
Province
Ontario
DATE DE DÉBUT
2024